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View our 2023 team members

Team funds raised: $55,943 Shalonda Alexander Team TSC VIEW MY PAGE Phil Iffland Team TSC VIEW MY PAGE Holly Knight Team TSC VIEW MY PAGE Shelly Meitzler Team TSC VIEW

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Ways to give

A gift to the TSC Alliance will make a tangible difference in the lives of those affected by tuberous sclerosis complex (TSC) in a variety of ways. Please look at

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Give at work

Matching gifts and volunteer grants Matching gifts can double or triple the size of a gift and are an important source of support for the TSC Alliance. If you or

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Become a member

The TSC Alliance is a membership-based organization, which means members participate in the corporate governance of the organization, which includes electing the Board of Directors. As such, members have a

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Awareness proclamations

Getting your mayor or even your state’s governor to declare May 15 as Tuberous Sclerosis Complex Awareness Day is one great way to ensure local officials not only know about

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State and local advocacy

Since 2014, state funding for TSC clinical care and research has been secured in Michigan, Missouri, Maryland and Alabama. Opportunities to advocate for state funding vary state-by-state. Learn more about

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Federal advocacy

The TSC Alliance advocates for increased financial support of TSC initiatives through the following federal agencies: The Tuberous Sclerosis Complex Research Program (TSCRP) at the Congressionally Directed Medical Research Program

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Government advocacy

Your voice makes a difference! $121 million appropriated for the TSCRP since 2002 $5.725 million to support clinical care and research at TSC centers in four states 120 volunteer advocates

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List of current sites

Boston Children’s Hospital, Boston, MA (Mustafa Sahin, MD, PhD) Children’s Hospital Colorado, Aurora, CO (Susan Koh, MD) [database only] Children’s National Medical Center, Washington, DC (William McClintock, MD) Cincinnati Children’s

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Patient-focused drug development

The TSC Alliance sponsored a patient-focused drug development meeting (PFDD) with the FDA on June 21, 2017. The purpose of this meeting was for individuals affected by TSC and caregivers

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Keith Hall Distinguished Leadership Award

In honor of Keith Hall’s legacy, the TSC Alliance created the Keith Hall Distinguished Leadership Award. The annual recipient of this award will be an adult with TSC whose efforts

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Community Region of the Year Award

The Community Region of the Year Award (renamed the Dreamer Award in 2016 in honor of Dee Triemer) is given to one outstanding Community Region that has made significant contributions

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Volunteer of the Year Award

The Volunteer of the Year (named the Franny Award in memory of Francine Ostrow) is an award given to up to four outstanding volunteers who have made significant contributions as

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Participate in research

The tuberous sclerosis complex (TSC) community is pivotal to advancing research. When you enroll in a clinical trial, share your medical data, donate biosamples or give voice to your lived

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Volunteer

Champion our cause:  Join the TSC Alliance volunteer movement! The tuberous sclerosis complex (TSC) community is the TSC Alliance’s strongest ally. We rely on our dedicated volunteers to help drive

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Transition workshops

Two one-day Transition Workshops in 2024 will feature local clinicians and consultants with expertise in the transition from pediatric to adult health care, as well as the transitions from postsecondary

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Adult topic calls

Adult topic calls provide a forum for independent or semi-independent adults with TSC to connect with other adults via Zoom and learn from experts on a wide array of relevant

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Future Leaders Program

Future Leaders are a group of individuals ages 17 through 27 including young adults with TSC, siblings of someone with TSC, or other relatives of someone with TSC who are

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Adult Support and Resource Leads

Adult Support and Resource Leads (formerly Adult Regional Coordinators) establish and cultivate new and existing relationships with adults with TSC in their community region to maximize their independence by offering

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Self-care & mental health

Being diagnosed with tuberous sclerosis complex (TSC) can cause significant challenges within the life of the individual regardless of when first diagnosed. It is essential to understand acknowledging that life

FAQ

Grief & bereavement

All caregivers should prepare for the possibility of grief or bereavement during the care of a loved one. Caregivers naturally become deeply emotionally invested in the individuals for whom they

FAQ

Caregiver mental health

Being a caregiver can be equally rewarding and overwhelming at the same time – it is completely normal to feel this way. Many caregivers start this journey as parents, yet

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SUDEP awareness

SUDEP stands for sudden unexpected death in epilepsy. It is a rare but fatal complication of epilepsy with no other known cause of death. While the exact cause of SUDEP is unknown, there are ways

FAQ

Residential & group homes

During the transition phase and estate planning, families ought to consider housing options that would best serve the needs of their loved one with tuberous sclerosis complex (TSC). As these

FAQ

Guardianship

A guardianship – or conservatorship depending on the state – is a legal action that grants an adult legal power to make decisions for another person. Guardianship is a legal

FAQ

Estate & financial planning

What is estate and financial planning? This topic can seem overwhelming with the breadth of information available on the topic. This guide will help you get familiar with the process

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Connect with a Support Navigator

Our professional Support Navigators can help guide you along your unique journey. They can help answer your questions, process, and understand your diagnosis, help find TSC recognized specialists, and discuss

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Adult support

Being diagnosed with tuberous sclerosis complex (TSC) can cause significant challenges within your adult life regardless of when you first received your diagnosis. The TSC Alliance is here to help.

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Community support network

The TSC Alliance is supported by a corps of dedicated volunteer leaders across the country. Whether you are dealing with a new diagnosis or are looking for local resources, they

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Educational support

The TSC Alliance recognizes parents and young adults often face many educational and school-related difficulties. The first step in becoming an advocate is understanding your child’s legally protected rights. The

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Bcureful travel & lodging assistance

The Bcureful Travel Fund® at the TSC Alliance underwrites the TSC Travel and Lodging Patient Assistance Program, which is administered by the National Organization for Rare Disorders (NORD). This travel

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Find Support

Connect with TSC Alliance support navigators, our volunteer support network and TSC clinicians to help guide you along your unique journey. Click on a link below to learn more. FIND

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Working with your healthcare team

You do not need to have all the answers or become an expert in TSC to navigate you/your loved one’s care. You can empower yourself by clearly advocating your understanding

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Starting a new treatment plan

Navigating a new treatment plan can elicit mixed emotions – on one hand, starting a new plan may seem daunting, while on the other, a change can provide hope and

FAQ

Medical access issues

Living with a rare disease is difficult and there will be challenging barriers throughout the journey. Challenges are commonly centered around limited local resources, structural barriers to access care, insurance

FAQ

Choosing a healthcare provider

It is common for medical providers to be unfamiliar with TSC, including neurologists, pediatricians and primary care providers (PCPs). It is crucial to have a local healthcare team involved in

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Psychosocial cluster recommendations

Monitor the psychosocial health and wellbeing of all individuals with TSC. Monitor the psychosocial functioning of all family members who live with TSC. Provide integrated and well-coordinated care to families

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TAND clusters and recommendations

While TSC impacts everyone differently, research analyzing TAND Checklist data identified seven natural clusters of TAND manifestations, as well as a wraparound psychosocial cluster. As stated above in the core

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The TAND Checklist

The TAND Checklist was developed to help clinical teams, individuals with TSC and their families screen for TAND and prioritize what to do next. Experts at the 2012 TSC Clinical

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The TAND Consortium and TANDem Project

The TAND Consortium is an international group of TSC experts including researchers, clinicians and TSC family representatives. TANDem is an international multi-disciplinary mobile-health project to empower families and individuals who

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Scholastic cluster recommendations

Scholastic difficulties are common in TSC and should receive early and ongoing screening, followed by appropriate action. Delays in language development, counting, social/communication skills, and other developmental milestones may be

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Overactive/Impulsive cluster recommendations

Overactive and impulsive behaviors are common in TSC and should be monitored in all individuals to ensure early detection and treatment All individuals with overactive and impulsive behaviors should be

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Neuropsychological cluster recommendations

Everyone with TSC should receive a comprehensive assessment of their intellectual ability at the time of diagnosis to identify their profile of strengths and weaknesses. Children and adults with TSC

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Mood/anxiety cluster recommendations

Mood and anxiety symptoms should be monitored in all children and adults with TSC to ensure early detection and treatment when necessary. Efforts should be made to look for mood

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Eat/sleep cluster recommendations

Eating difficulties do occur in TSC and could be related to a range of TAND and physical health issues. Therefore, eating difficulties should be monitored on a regular basis. As

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Dysregulated behavior cluster recommendations

Dysregulated behaviors are common in TSC, have a major impact on the family and require a systematic approach. It is important to understand the meaning/function of dysregulated behaviors to guide

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Dysregulated behaviors

Dysregulated behaviors, including aggression, temper tantrums, and self-injury, represent the greatest concerns and burdens to families who live with TSC. These behaviors are therefore a common reason for referral to

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Autism-like cluster recommendations

Everyone with TSC should be monitored for symptoms in the autism-like cluster from early in infancy and throughout adulthood. Anyone who shows behaviors within the autism-like cluster should be referred

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Types of pharmacies

In addition to your primary care physician and team of specialists, your local pharmacist and insurance case manager are important members of your healthcare team. Being proactive in establishing these

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Overcoming hurdles

Webinar In January 2021, the TSC Alliance hosted an educational webinar with Greenwich Biosciences titled “Overcoming Hurdles: Insurance, Scripts and Specialty Pharmacy.”  You may watch it below or at this

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Assistance programs

Many medications have co-pay assistance programs for those who qualify. Generally, co-pay assistance is for commercial insurance plans. However, drug manufacturers may also have patient assistance programs (PAPs) for those

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Tips to mitigate issues

Medication denials by insurers are an unfortunate reality that can occur. It is helpful to understand why many denials are made and what can be done to prevent them. Usually,

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Prior authorization issues

Medications prescribed for TSC-related manifestations often require a prior authorization (PA). It is important to know what medications will require this, and how long the PA is approved for each

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Pharmacy coverage

Prescription drug plans are part of all commercial and government insurance plans in the United States; however, each plan is different per corporation / organization and state. When starting to

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Medication access issues

Many people with tuberous sclerosis complex (TSC) rely on several medications to treat different manifestations of the disease. Disruptions to medication can have negative impacts on an individual with TSC

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Pharmacy Resources

Medication Access Issues Medication Resources Types of Pharmacies

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Self-care & Mental Health

Being diagnosed with tuberous sclerosis complex (TSC) can cause significant challenges within the life of the individual regardless of when first diagnosed. It is essential to understand acknowledging that life

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Grief & Bereavement

All caregivers should prepare for the possibility of grief or bereavement during the care of a loved one. Caregivers naturally become deeply emotionally invested in the individuals for whom they

FAQ

The aging caregiver

Growing old is an inevitable part of life, but it can be especially daunting for those who care for individuals with a rare disease and/or intellectual disabilities. Life as a

FAQ

Transition planning

Regardless of their disabilities, all children eventually become adults – both physically and legally. Transition planning is an intentional and coordinated process used to help students with disabilities transition from

FAQ

Skin, eyes & teeth manifestations

Most of these manifestations do not cause life-altering problems. However, facial angiofibromas do continue to grow throughout this part of the lifespan and can become painful and cause recurrent bleeding

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Heart manifestations

Typically during adulthood the common pediatric manifestation of cardiac rhabdomyomas has completely regressed. However, some individuals with TSC will continue to have small evidence of these lesions throughout adulthood. There

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Lung manifestations

Individuals with TSC are at a higher risk of developing lymphangioleiomyomatosis (LAM). LAM is a rare lung disease that affects women more often than men, usually between the onset of

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End-stage renal disease

End-stage renal disease (ESRD) is when your kidneys permanently stop working and require long-term dialysis or a kidney transplant to maintain life. While ESRD is rare in TSC, chronic kidney

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Kidney manifestations

Kidney (renal) manifestations such as cystic disease and renal angiomyolipomas continue to grow throughout this part of the lifespan. Not only are you/your loved one aging, in which chronic kidney

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Transition & Adult Years

As people with tuberous sclerosis complex (TSC) age and transition from pediatrics to adult care, certain manifestations which may or may not have been problematic during childhood or adolescence now

FAQ

Heart manifestations

The common pediatric manifestation of cardiac rhabdomyomas is known to regress over time from birth. However, some individuals with TSC will continue to have small evidence of these lesions throughout

FAQ

Lung manifestations

Individuals with TSC are at a higher risk of developing lymphangioleiomyomatosis (LAM). LAM is a rare lung disease that affects women more often than men, usually between the onset of

FAQ

Kidney manifestations

Kidney (renal) manifestations such as cystic disease and renal angiomyolipomas continue to grow throughout this part of the lifespan. Not only is your loved one aging, in which chronic kidney

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Neurological manifestations

During infancy through young adulthood seizures and subependymal giant cell astrocytoma (SEGA) dominate much of the medical journey. Seizures are still problematic for many and unfortunately several have developed refractory

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Early & Childhood Years

It is common for medical providers to be unfamiliar with tuberous sclerosis complex (TSC), including neurologists and pediatricians. It is crucial to have a local neurologist and pediatrician involved in

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SUDEP Awareness

SUDEP stands for sudden unexpected death in epilepsy. It is a rare but fatal complication of epilepsy with no other known cause of death. While the exact cause of SUDEP

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Residential & Group Homes

During the transition phase and estate planning, families ought to consider housing options that would best serve the needs of their loved one with tuberous sclerosis complex (TSC). As these

FAQ

Guardianships

A guardianship – or conservatorship depending on the state – is a legal action that grants an adult legal power to make decisions for another person. Guardianship is a legal

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Estate & Financial Planning

What is estate and financial planning? This topic can seem overwhelming with the breadth of information available on the topic. This guide will help you get familiar with the process

FAQ

Tips from adults

Along your journey, it is helpful to know you are not alone. Despite this being a very difficult time, the TSC community has compiled helpful resources to guide you during

FAQ

Where do I go?

It is common for medical providers to be unfamiliar with TSC, including neurologists, and primary care providers (PCPs). It is crucial to have local healthcare team involvement in your care

FAQ

What are my options?

Treatment options directly depend on the manifestation or the organ system that is causing an issue. Adulthood diagnosis of TSC typically presents much differently than childhood, therefore treatment management is

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Where do I start?

In adulthood this can be by an incidental finding (meaning it was found by looking for something else) or an abrupt finding (such as a renal hemorrhage) which can be

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Tips from parents

Along your journey, it is helpful to know you are not alone. Despite this being a very difficult time, the TSC community has compiled helpful resources to guide you during

FAQ

Where do I go?

It is common for medical providers to be unfamiliar with TSC, including neurologists, and pediatricians. It is crucial to have a local neurologist and pediatrician involved in your child’s healthcare

FAQ

What are my options?

Treatment options directly depend on the manifestation, such as the type of seizure or the organ system that is causing an issue. If your child presented with seizures, the most

FAQ

Where do I start?

Often, a TSC diagnosis can be sudden which can be even more overwhelming to process – there can be an immense amount of testing and specialist visits to coordinate all

FAQ

Tips from parents

Along your journey, it is helpful to know you are not alone. Despite this being a very difficult time, the TSC community has compiled helpful resources to guide you during

FAQ

In utero diagnosis

The most common manifestation in utero are irregular growths in heart tissue, known as cardiac rhabdomyoma. These are benign (non-cancerous) and usually get smaller on their own as the child ages.  Rhabdomyomas

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Prenatal screening

Prenatal genetic testing is a common method many women seek to learn whether their baby has certain genetic disorders. There are two types of prenatal tests, prenatal screening tests and

FAQ

Evaluation of new-onset seizures in adults 

All individuals with new-onset seizures should request a referral to a neurologist, preferably one who is an epileptologist with knowledge of TSC. This neurologist will perform a complete neurological exam,

FAQ

What is status epilepticus?

The official definition of status epilepticus has evolved over time, but the term generally refers to a prolonged seizure that may not stop on its own without intervention. The most recent definition

FAQ

What is a seizure cluster?

The definition of a seizure cluster varies from one individual to another, but in general the term refers to a group of seizures occurring over a number of hours or days in

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Seizure clusters & status epilepticus

Epilepsy is a very common manifestation of tuberous sclerosis complex (TSC), occurring in 84% of patients registered in the TSC Alliance Natural History Database. Potential complications of epilepsy include seizure

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Epilepsy treatment options

Epilepsy is a common manifestation of tuberous sclerosis complex (TSC). More than 80% of individuals with TSC will have seizures at some point during the journey, most often beginning in

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Infantile spasms

Infantile spasms or epileptic spasms are severe seizure disorders that may affect infants with tuberous sclerosis complex (TSC). About 30% of children with TSC may start experiencing these seizures. The

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Brain abnormalities

Several types of brain abnormalities may be seen in individuals with tuberous sclerosis complex (TSC), including cortical tubers, subependymal nodules (SEN), and subependymal giant cell astrocytoma (SEGA). Some individuals will

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Working with Your Healthcare Team

You do not need to have all the answers or become an expert in TSC to navigate you/your loved one’s care. You can empower yourself by clearly advocating your understanding

Page

Starting a New Treatment Plan

Navigating a new treatment plan can elicit mixed emotions – on one hand, starting a new plan may seem daunting, while on the other, a change can provide hope and

Page

Medical Access Issues

Living with a rare disease is difficult and there will be challenging barriers throughout the journey. Challenges are commonly centered around limited local resources, structural barriers to access care, insurance

Page

Choosing a Healthcare Provider

It is common for medical providers to be unfamiliar with TSC, including neurologists, pediatricians and primary care providers (PCPs). It is crucial to have a local healthcare team involved in

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Bones

Sclerotic bone lesions are commonly observed in individuals with tuberous sclerosis complex (TSC) when high-resolution chest computed tomography (CT) is performed as surveillance for possible lymphangioleiomyomatosis (LAM) or abdominal magnetic

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Other organs

Cysts and angiomyolipomas similar to those found in the kidneys have been observed in other organs, such as the adrenal gland, liver, lung, ovary and pancreas. These lesions are usually

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Teeth

Oral involvement in TSC can include gum fibromas and dental pits. The fibromas appear as overgrowth of the gums and can be quite extensive, although this finding is not common

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Heart

Tumors in the heart called rhabdomyomas are common in infants with tuberous sclerosis complex (TSC), affecting an estimated 47-67% of infants with TSC. Rhabdomyomas can affect cardiac function in some

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Lungs

Lung involvement is more common in women with TSC than men. The average age of onset is during the childbearing years, although lung involvement can occasionally occur in teenagers with

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Skin

Most people with tuberous sclerosis complex (TSC) have changes in their skin. Nearly all people with TSC develop at least one skin feature during their lifetime, and many will have

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Kidneys

Most individuals (greater than 80%) with tuberous sclerosis complex (TSC) will develop some form of renal (kidney) disease during their lifetime. There are three renal disorders in TSC: renal cysts,

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Eyes

Nearly 50% of individuals with TSC have involvement of one or both eyes, but visual loss is uncommon. This may be higher as many individuals with TSC do not receive

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Epilepsy/seizure disorders

One of the most common neurological features of tuberous sclerosis complex (TSC) are seizures. This feature occurs in 84% of individuals with TSC. In some cases, seizures can start as

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Brain & neurological function

Multiple manifestations can occur in the brain of someone with TSC. Click on an item listed below to learn more: Brain abnormalities  Epilepsy/seizure disorders In addition to these physical challenges,

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Surveillance & treatment

The following table provides guidelines to help you and your loved one manage the treatment of TSC. Additional information for your physician is available here. Surveillance & management recommendations for TSC

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Diagnostic criteria

In 2021, the International Tuberous Sclerosis Complex Consensus Group reviewed prevalence and specificity of TSC-associated clinical manifestations and updated the TSC diagnostic criteria published in 2013. Clinical features of TSC

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Prognosis

Most people with TSC will live a normal life span. Although there is no cure, there is hope. Research has proven that early diagnosis and intervention(s) are key for optimizing

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Clinical Manifestations

Because TSC affects no two people the same, there is no sure way to predict where and how the disorder will manifest. To better understand its potential impact, click below

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Genetics

TSC affects multiple organs throughout the lifetime. Both the TSC1 and TSC2 genes hold the instructions for creating proteins called hamartin and tuberin, respectively.  These proteins form a complex (essentially

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Stories of hope

While no one’s experience with tuberous sclerosis complex (TSC) is exactly the same, there are common threads the TSC community shares: overcoming adversity, finding joy in moments small and large,

Story of Hope

Megan Elizabeth Self

I was diagnosed with TSC at birth and although I have a mild case of TSC, I have endured many challenges.  I have a Bachelor of Science in Health Sciences

Story of Hope

Shae Sunahara

Shae was diagnosed with TSC when she was 3 months old. Over the years, she’s taken special education classes, including life skills courses focusing on transitioning into adulthood. She also

Story of Hope

Amaan Panjwani

Amaan was diagnosed with TSC when he was 5 months old. He’s currently a Junior at Creekview High School. He likes to take one day at a time and “always

Story of Hope

Keira Luke

When Keira was born with TSC, the meaning of life for her mother, Sunny, was forever changed. Sunny is blind due to retinitis pigmentosa. Sunny had to learn how to

Story of Hope

Terrence Hamilton, Jr.

Terrence was diagnosed with TSC when he was 3 days old. He is home schooled and is in the 10th grade, living at home with his parents. He is passionate about

Story of Hope

Max Lucca Bertolotti

Diagnosed with TSC at two weeks old, Max is currently in the 8th grade. He has TSC1 and was born with multiple tubers in his brain, a SEGA brain tumor,

Story of Hope

Chloe Carpenter

Chloe was found to have an irregular heartbeat at 12 hours old, with an MRI confirming her TSC diagnosis at 36 hours. She is currently a very happy and engaged

Story of Hope

Emmaus Ballew

Emmaus was diagnosed with TSC at birth, while several cardiac rhabdomyomas were found at 34 weeks gestation. Emmaus has epilepsy and autism and is currently a fourth grader with an

Story of Hope

Arij Chattopadhyay

Diagnosed at 10 days before birth, Arij started second grade recently. His first few years were hard and overwhelming for him and his family, although they know all families have

Story of Hope

Noah Johnson

Noah was diagnosed with TSC at birth. His parents say, “Noah has hope, because so many individuals, whom we may never know their names and get to thank personally, have

Story of Hope

Seraphina Holmes

Seraphina was diagnosed in utero and is currently in pre-school. Seraphina’s mom Lesley says, “Never give up hope. Seraphina’s diagnosis has taught our family to take nothing for granted and to

Story of Hope

Jovee Shae Dreier

TSC was suspected at 23 weeks in utero due to cardiac rhabdomyomas identified during a routine ultrasound. Her diagnosis of TSC2 was confirmed through genetic testing of her cord blood,

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Caregiver resources

Embarking on the caregiver journey for individuals with tuberous sclerosis complex (TSC) involves thoughtful consideration and planning. The sections below provide valuable insights into key aspects that caregivers often navigate.

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Coordination of care

Navigating tuberous sclerosis complex (TSC) involves adopting a strategic healthcare approach. As medical providers often lack familiarity with TSC, it’s crucial to form a local healthcare team to serve as

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Surveillance & management

Managing tuberous sclerosis complex (TSC) across the lifespan requires attentive surveillance and effective strategies. Delve into the challenges and considerations present in both the early and childhood years, as well

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Mental health

Caregivers and individuals with tuberous sclerosis complex (TSC) often meet challenges, and mental health plays a crucial role in navigating these complexities. This section explores valuable insights and resources for

Testimonial

Donato Family

“A blood draw is such an easy thing for my daughter to do. To have it done at home makes it super convenient.”

News Item

New publication on International consensus recommendations for TAND

International consensus recommendations for the identification and treatment of tuberous sclerosis complex-associated neuropsychiatric disorders (TAND) from researchers from the TANDem project were recently published in the Journal of Neurodevelopmental Disorders.

News Item

Sabril Supply Issue Recommendations

The TSC Alliance® is aware of the current supply issue with Sabril Oral Solution, 500 mg packets; it does NOT affect Sabril tablets 500mg. Lundbeck estimates this issue will be

FAQ

Corporate Relations Policy

The TSC Alliance will enter into corporate relationships for the sole purpose of providing mission related benefits to its members and the TSC community. The TSC Alliance will not accept

FAQ

Financial Conflict of Interest Policy

The Public Health Service (PHS) has adopted regulations (42 CFR Part 50 Subpart F and 45 CFR Part 94) to provide a reasonable expectation that the design, conduct, and reporting

Team Member

Sam Metzger

Sam joined the TSC Alliance in July 2023 as a Scientific Project Manager. While attending George Washington University, from which she graduated with a Bachelors of Science in Biology, she

Team Member

Elizabeth Skufca

Elizabeth joined the TSC Alliance in June 2023 as Community Programs Manager. She brings a wealth of experience working with young people and families from her career as a middle

TSC Matters Post

April 2023 Message from the CEO

TSC Alliance President & CEO Kari Luther Rosbeck announces registration opening for the 2023 Regional TSC & LAM Conference Series co-hosted with The LAM Foundation, encourages everyone to participate in

TSC Matters Post

Congratulations to our Volunteers of the Year

Earlier this year, as part of our Volunteer Leadership Summit, the TSC Alliance recognized several volunteers for their outstanding dedication and commitment to our organization and for tireless efforts supporting TSC individuals

TSC Matters Post

Current Clinical Trials

See below for ongoing clinical trials. For a full list of clinical trials go to the Clinical Trial Finder to find a trial that may best suit your needs.

TSC Matters Post

Anya’s Accelerator TAND Biomarker Workshop

With support from the The Ramesh and Kalpana Bhatia Family Foundation, the TSC Alliance hosted the first Anya’s Accelerator TAND Biomarker Workshop April 26-27, 2023 in Silver Spring, MD.

Resource

Episode 44: Rare Conversations

Disclaimer: This episode is sponsored by Nobelpharma America LLC. The opinions expressed are those of the host and guest speaker individually and do not reflect the policies or positions of

Testimonial

Ridler Family

“We want to see a cure in our lifetime and have to say things are so much better than 30 years ago because of the efforts of researchers and the TSC Alliance.”

TSC Matters Post

We Need Your Input!

In 2023, the TSC Alliance will update our five-year strategic plan, so we are launching a comprehensive online Constituent Survey to assess what the organization is doing right, identify those

Resource

Episode 42: Understanding Seizure Clusters

In the first episode of TSC Now in 2023, host Dan Klein recognizes International Epilepsy Day (February 13, 2023) and Seizure Action Plan Awareness Week (February 13-20, 2023) by learning

FAQ

View our 2022 team members

Team funds raised: $27,172 Chip Burkhalter Team Bear Goal: $5,000 Amount Raised: $8,589 Thomas Peter Crino Goal: $5,000 Amount Raised: $5,923 Thomas Jenny Kuehn Team TSC Runs! Goal: $5,000 Amount

FAQ

View our 2021 Team Members

Team funds raised: $47,654 Claire Blyth Running for Revi Goal: $5,000 Amount Raised: $6,689 1246142 Balance Chip Burkhalter Team Bear Goal: $5,000 Amount Raised: $6,482 Thomas Kristin Burkhalter Team Bear

Team Member

Maddison Larrimore

Maddison joined the TSC Alliance in January 2023 as Social Media & Content Coordinator. She brings four years of content creation and social media experience contributing to her role with

Resource

Episode 41: Help Today, Help Tomorrow

In the final episode of TSC Now in 2022, host Dan Klein connects with two incredible advocates for individuals with disabilities and learns how families can find support to help

Team Member

Liz Cassidy, MPH

Liz joined the TSC Alliance in October 2022. She has previous clinical research experience, including undergraduate research experience at The Catholic University of America, where she graduated in 2018. As an undergrad,

Resource

Episode 40: Totally Super Cool!

In a special bonus episode of TSC Now, host Dan Klein learns about a new children’s book called Totally Super Cool, which was developed by Nobelpharma America, LLC. This Podcast

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En Español

Bienvenido a la página de la TSC Alliance; la alianza que sirve como una fuente de esperanza y apoyo para las personas con el complejo de esclerosis tuberosa (CET) y

Testimonial

Leonard/Grabb Family

“Our family chose to participate in this initiative because we have seen the progress made over our son’s lifetime due to research advances.”

Testimonial

Gomes Family

“I chose to participate in the Biosample Repository because I was asked by caring people in similar situations and it is the right thing to do for her.”

TSC Matters Post

Message from the CEO – April 2022

TSC Alliance® President and CEO Kari Luther Rosbeck, along with Director of Community Education & Resources Shelly Meitzler, Vice President of Community Programs April Cooper, and World TSC Conference Chair

Team Member

Carly Kaye

Carly joined the TSC Alliance as Community Programs Manager in April 2022 after serving as a volunteer including Chair, TSC Alliance of Michigan, and Clinic Ambassador at the TSC Clinic

Team Member

Rachel Wojnilower

Rachel joined the TSC Alliance in March 2022 and currently serves as the TSC Alliance’s Chief of Staff. In her role, she serves as a liaison between the President and

Team Member

Ryan Beebe

Ryan joined the TSC Alliance in March 2022 as Manager, Annual Giving & Partnerships.  In this role, Ryan assists in the overall strategic planning and managing of the organization’s strategic

Testimonial

Meitzler Family

“It’s super easy and convenient right in our house.”

Testimonial

Brtan Family

“We highly recommend any parent or TSC adult to participate in the process to seek cure of TSC.”

Testimonial

Sunahara Family

“By participating in the Tuberous Sclerosis Complex Research and the Biosample Repository Program, we know we will bring new hope for patients afflicted, no matter how immediate.”

Testimonial

Parkes Family

“We are so grateful for the many advances in TSC Research and for the patients and parents who have offered data and samples, contributing to this great progress.”

TSC Alert

DSC Funding Opportunity – DEADLINE APRIL 15!

The Pilot Feasibility Core of the Developmental Synaptopathies Consortium (DSC) is pleased to announce it will fund an estimated $30,000 total costs per project (three in total) to stimulate additional research

Testimonial

Russell Family

“The TSC Alliance’s mobile phlebotomy initiative made it easy for our daughter to participate safely and in the comfort of our own home.”

Team Member

Cynthia Arcuri, CPA

Cynthia joined the TSC Alliance team in January 2022 and previously served as Director of Finance & Administration at a public accounting firm in Pittsburgh, PA, overseeing all firm operations,

Team Member

Anne Wolfe

Anne joined the staff in 2021 as Senior Community Programs Manager and was promoted to Senior Manager of Strategic Projects in January 2023. In this role, she oversees a portfolio

Team Member

Christen Bell

Christen joined the TSC Alliance as a grant writer consultant in July 2021. She has three years of freelance writing experience, including research and a variety of content creation and

TSC Matters Post

Thank You Future Leaders Class of 2020-2021

The six young adults in the Future Leaders Class of 2020-2021 greatly exceeded the requirements of the program and have been instrumental in moving it forward. Too often young adults

Resource

Episode 28: Comedy for a Cure® 2021!

In a very special episode of TSC Now, host Dan Klein provides a sneak peek of the 19.5 Annual Comedy for a Cure® on Sunday October 17 at 7:30 pm

TSC Matters Post

August Volunteer Opportunities

Champion Our Cause: Join the TSC Alliance Volunteer Movement “The smallest act of kindness is worth more than than the grandest intention.”  – Oscar Wilde The TSC Alliance thrives on the

TSC Matters Post

June Volunteer Opportunities Available

Champion Our Cause: Join the TSC Alliance Volunteer Movement “The smallest act of kindness is worth more than than the grandest intention.”  – Oscar Wilde The TSC Alliance thrives on the

TSC Alert

New Free CME Opportunity Available

Hear leading experts in tuberous sclerosis complex (TSC) discuss recent updates to consensus recommendations and offer practical guidance for the diagnosis, surveillance, and management of TSC in a new CME-certified

TSC Alert

New Free CME Opportunity Available

Hear leading experts in tuberous sclerosis complex (TSC) discuss recent updates to consensus recommendations and offer practical guidance for the diagnosis, surveillance, and management of TSC in a new CME-certified

TSC Alert

What’s With the New Look?

On Sunday May 16, the Tuberous Sclerosis Alliance formally unveiled a new brand and new name: TSC Alliance. We also introduced a new tagline, “Hope no matter how complex.”

TSC Matters Post

April 2021 Note from the President & CEO

TSC Alliance President and CEO Kari Luther Rosbeck provides organizational updates, including: How you can get involved in the upcoming Step Forward to Cure TSC Global Virtual Walk-Run-Ride. Information on

TSC Matters Post

Congratulations to Our 2020 Volunteers of the Year!

On Friday, March 5 the TSC Alliance hosted our annual Volunteer Appreciating Celebration to pay tribute to the outstanding work of our incredible volunteers, who continue to work diligently around

TSC Matters Post

April Volunteer Opportunities Available

Champion Our Cause: Join the TSC Alliance Volunteer Movement “The smallest act of kindness is worth more than than the grandest intention.”  – Oscar Wilde The TSC Alliance thrives on the

TSC Alert

Clinical Trial Finder Tool

The TSC Alliance has partnered with Clinical Trial Connect to develop a user-friendly Clinical Trial Finder Tool to help individuals and families affected by TSC participate in relevant clinical trials.

TSC Matters Post

February Volunteer Opportunities Available

Champion Our Cause: Join the TSC Alliance Volunteer Movement “The smallest act of kindness is worth more than than the grandest intention.”  – Oscar Wilde The TSC Alliance thrives on the

TSC Matters Post

Curing the Epilepsies Conference Summary

The National Institute of Neurological Disorders and Stroke (NINDS) has sponsored a Curing the Epilepsies conference every seven years in 2000, 2007, and 2013. A major outcome of these conferences

TSC Matters Post

In Memory Of Ken Johnson

The TSC Alliance and Endowment Fund Board of Directors recently established the Ken Johnson Memorial Fund to honor and pay tribute to Ken Johnson – a grandparent, organizational leader, compassionate volunteer

TSC Alert

Clinical Trial Finder Tool

The TSC Alliance has partnered with Clinical Trial Connect to develop a user-friendly Clinical Trial Finder Tool to help individuals and families affected by TSC participate in relevant clinical trials.

TSC Alert

New Clinical Trial Finder Tool

The TSC Alliance has partnered with Clinical Trial Connect to develop a user-friendly Clinical Trial Finder Tool to help individuals and families affected by TSC participate in relevant clinical trials.

TSC Matters Post

December Volunteer Opportunities Available

Champion Our Cause: Join the TSC Alliance Volunteer Movement “The smallest act of kindness is worth more than than the grandest intention.”  – Oscar Wilde The TSC Alliance thrives on the

TSC Matters Post

Welcome from Nobelpharma America!

Nobelpharma America is the first global subsidiary of Nobelpharma Co. Ltd (“Nobelpharma”), headquartered in Tokyo, Japan. Founded in 2003, Nobelpharma received its first drug approval in Japan in 2008. Since

TSC Matters Post

December Note from the CEO

      In the last edition of TSC Matters back in October, I reflected on all the ways the COVID-19 pandemic has challenged our organization to pivot and how

TSC Alert

New Clinical Trial Finder Tool

The TSC Alliance has partnered with Clinical Trial Connect to develop a user-friendly Clinical Trial Finder Tool to help individuals and families affected by TSC participate in relevant clinical trials.

TSC Alert

New Clinical Trial Finder Tool

The TSC Alliance has partnered with Clinical Trial Connect to develop a user-friendly Clinical Trial Finder Tool to help individuals and families affected by TSC participate in relevant clinical trials.

TSC Matters Post

October Note from the CEO

      This year has challenged us to come up with new ways to bring our community together, to empower those living with TSC and their loved ones and

TSC Matters Post

October Volunteer Opportunities Available

Champion Our Cause: Join the TSC Alliance Volunteer Movement “The smallest act of kindness is worth more than than the grandest intention.”  – Oscar Wilde The TSC Alliance thrives on the

TSC Matters Post

Join Us for an Upcoming Adult Topic Call

Are you an independent or semi-independent adult with TSC? If so, please join us for our upcoming free informational adult calls! You can join the call using your computer or dialing

TSC Alert

New Clinical Trial Finder Tool

The TSC Alliance has partnered with Clinical Trial Connect to develop a user-friendly Clinical Trial Finder Tool to help individuals and families affected by TSC participate in relevant clinical trials.

TSC Alert

New Clinical Trial Finder Tool

The TSC Alliance has partnered with Clinical Trial Connect to develop a user-friendly Clinical Trial Finder Tool to help individuals and families affected by TSC participate in relevant clinical trials.

Resource

Episode 16: COVID-19 and Back to School

In episode 16 of TSC Now, host Dan Klein talks to two of the TS Alliance’s Education Parent Mentors to better understand how parents should approach making the decision on

TSC Matters Post

Epilepsy Trial

Adjunctive Ganaxolone Treatment (Part A) in TSC Followed by Long-term Treatment (Part B) Study Purpose To assess preliminary safety and efficacy of ganaxolone as adjunctive therapy for the treatment of

TSC Matters Post

August Volunteer Opportunities Available

Champion Our Cause: Join the TSC Alliance Volunteer Movement “The smallest act of kindness is worth more than than the grandest intention.”  – Oscar Wilde The TSC Alliance thrives on the

TSC Alert

New Clinical Trial Finder Tool

The TSC Alliance has partnered with Clinical Trial Connect to develop a user-friendly Clinical Trial Finder Tool to help individuals and families affected by TSC participate in relevant clinical trials.

TSC Alert

New Clinical Trial Finder Tool

The TSC Alliance has partnered with Clinical Trial Connect to develop a user-friendly Clinical Trial Finder Tool to help individuals and families affected by TSC participate in relevant clinical trials.

TSC Matters Post

Epilepsy Trial

Adjunctive Ganaxolone Treatment (Part A) in TSC Followed by Long-term Treatment (Part B) Study Purpose To assess preliminary safety and efficacy of ganaxolone as adjunctive therapy for the treatment of

TSC Matters Post

June Volunteer Opportunities Available

Champion Our Cause: Join the TSC Alliance Volunteer Movement “The smallest act of kindness is worth more than than the grandest intention.”  – Oscar Wilde The TSC Alliance thrives on the

TSC Alert

New Clinical Trial Finder Tool

The TSC Alliance has partnered with Clinical Trial Connect to develop a user-friendly Clinical Trial Finder Tool to help individuals and families affected by TSC participate in relevant clinical trials.

TSC Matters Post

April Volunteer Opportunities Available

Champion Our Cause: Join the TSC Alliance Volunteer Movement “The smallest act of kindness is worth more than than the grandest intention.”  – Oscar Wilde The TSC Alliance thrives on the

TSC Matters Post

April Note from the President & CEO

      It is crazy to think that six short weeks ago we were wrapping up an emotional and productive March on Capitol Hill and Spring Board Meeting, which

TSC Alert

New Clinical Trial Finder Tool

The TSC Alliance has partnered with Clinical Trial Connect to develop a user-friendly Clinical Trial Finder Tool to help individuals and families affected by TSC participate in relevant clinical trials.

TSC Alert

Reminder: Research Grant LOIs Due April 27

The TSC Alliance has extended the deadline to submit letters of intent for Postdoctoral Fellowships and Early Stage Investigator Research Grants. Learn more about our funding mechanisms and eligibility requirements

TSC Alert

Deadline Extended: Research Grant LOIs Due April 27

The TSC Alliance has extended the deadline to submit letters of intent for Postdoctoral Fellowships and Early Stage Investigator Research Grants. Learn more about our funding mechanisms and eligibility requirements

TSC Alert

New Clinical Trial Finder Tool

The TSC Alliance has partnered with Clinical Trial Connect to develop a user-friendly Clinical Trial Finder Tool to help individuals and families affected by TSC participate in relevant clinical trials.

TSC Alert

Early Stage Investigator Research Grant LOIs Due April 6

The TSC Alliance is now accepting letters of intent for Postdoctoral Fellowships and Early Stage Investigator Research Grants. Learn more about our funding mechanisms and eligibility requirements on our Grants page.

TSC Matters Post

February Volunteer Opportunities Available

Champion Our Cause: Join the TSC Alliance Volunteer Movement “The smallest act of kindness is worth more than than the grandest intention.”  – Oscar Wilde The TSC Alliance thrives on the

TSC Matters Post

February Global Alliance Update

Last week, TSC Alliance Director of Government & Global Affairs Katie Smith, along with TSC Clinic Director Darcy Krueger, MD, PhD of Cincinnati Children’s Hospital and TAND Unit Director Tanjala T. Gipson, MD

TSC Matters Post

February Note from the President and CEO

      Following what was a truly inspiring 45th anniversary year, all of us at the TSC Alliance started this new year motivated to capture that momentum and channel

TSC Alert

New Clinical Trial Finder Tool

The TSC Alliance has partnered with Clinical Trial Connect to develop a user-friendly Clinical Trial Finder Tool to help individuals and families affected by TSC participate in relevant clinical trials.

TSC Alert

Call for Grant LOIs

The TSC Alliance is now accepting letters of intent for Postdoctoral Fellowships and Early Stage Investigator Research Grants. Learn more about our funding mechanisms and eligibility requirements on our Grants page.

Resource

Episode 9: The State of the TS Alliance

In episode 9 of TSC Now, host Dan Klein talks to Tuberous Sclerosis Alliance President and Chief Executive Officer Kari Luther Rosbeck. They discuss her favorite memories from the organization’s

Team Member

Katie Smith

Katie joined the TSC Alliance staff in 2006.  She currently oversees the organization’s international outreach efforts, directs government advocacy efforts and co-chairs TSC International. During her tenure with the TSC

Team Member

Gail Saunders

Gail joined the TSC Alliance in 2005 as the Office Manager, providing administrative and logistical support for the staff and board of directors. Over the years, her enthusiasm grew for

Team Member

Lisa Moss

Lisa joined the TSC Alliance staff in July 2012 and oversees the TSC Alliance’s fundraising efforts to ensure the organization is able to provide essential support services, and drive research